RESEARCH TRIANGLE PARK, N.C. and PALO ALTO, Calif., April 29, 2025 (GLOBE NEWSWIRE) -- Kriya Therapeutics, Inc. ("Kriya"), a biopharmaceutical company developing gene therapies to address chronic ...

Title: Autologous human peripheral blood B cells genetically engineered to express human iduronidase: Results from a first-in-human clinical trial in subjects with mucopolysaccharidosis type I (MPS I) ...

The company’s exhibitions will be focused in the areas of its pipeline, proprietary capsid engineering, and manufacturing. Thousand Oaks, Calif.-based Capsida Biotherapeutics (Capsida) has announced ...

ASGCT–OTXL joint venture platform goes live with demo at ASGCT 2026 Annual Meeting and applications opening this month for qualified Asset listings The platform is being demonstrated live during the ...

The American Society of Gene and Cell Therapy (ASGCT) is the primary professional membership organization for gene and cell therapy. The Society's members are scientists, physicians, patient advocates ...

Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. NEW ORLEANS — The mood at the annual ...

Title: Successful In Vivo Oral Delivery of Biologically Active and Therapeutic Anti-Inflammatory mRNA-Targeted Oligonucleotides with a Lipid Nanocrystal Delivery Platform About the ASGCT Annual ...

More than 10,000 known rare diseases affect over 30 million people in the United States. However, treatment options have been restricted due to small patient populations and limited commercial ...

Findings show Mirai’s in vivo data-driven machine learning platform can optimize lipid nanoparticles for adipocyte delivery while reducing off-target delivery to liver and spleen Data highlight high ...

Hans-Peter Kiem, MD, PhD, who holds the Stephanus Family Endowed Chair for Cell and Gene Therapy, has been awarded the 2026 George Stamatoyannopoulos Mentorship Award by the American Society of Gene ...