As of May 2025, 62 active clinical trials are ongoing for Fabry disease, including 25 interventional and 37 observational studies, of which 8 are patient registries. Among the trials with known ...

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The researchers observed that the specific assessment method heavily influenced the prevalence estimates. Anxiety and depression are common among patients with idiopathic pulmonary fibrosis (IPF), and ...

Efficacy analyses for the first 2 cohorts of the phase 1/2 studies will compare participant outcomes with those of a propensity score-matched external control group. AMT-130, an investigational gene ...

Treatment with obexelimab compared with placebo was associated with a significantly longer time to the first IgG4-RD flare that required the use of rescue therapy (P .001). One hundred ninety-four ...