As of May 2025, 62 active clinical trials are ongoing for Fabry disease, including 25 interventional and 37 observational studies, of which 8 are patient registries. Among the trials with known ...
Efficacy analyses for the first 2 cohorts of the phase 1/2 studies will compare participant outcomes with those of a propensity score-matched external control group. AMT-130, an investigational gene ...
The researchers observed that the specific assessment method heavily influenced the prevalence estimates. Anxiety and depression are common among patients with idiopathic pulmonary fibrosis (IPF), and ...